# Sickle cell disease

1 posts.

- [One-time base editing for sickle cell disease met its goal of a year free of severe crises, Beam says](https://healthcarenews.io/news/base-editing-for-sickle-cell-disease.md) (2026-11-11): Beam says its one-time treatment using base editing for sickle cell disease met its pivotal goal of a year free of severe crises; an FDA filing may follow.

